Amicus Therapeutics and the Treatment of Rare Diseases

Amicus Therapeutics is a biotechnology company that focuses on researching treatment for rare and orphan diseases. Although the company is based in Cranbury, New Jersey, they operate a second research site in San Diego, California. Amicus was founded in 2002 but didn’t go public until 2007. The company is fairly small, with around five hundred employees. Amicus is primarily research based and has to have other companies take care of manufacturing. Although the company offers no products as of 2017, a few potential products are in the final stages of being approved for commercial use.

https://seekingalpha.com/article/4073303-amicus-therapeutics-small-biotech-seems-big-mo

Fabry Disease is one illness that Amicus Therapeutics is currently researching. The company has developed two potential products to help treat it: Galafold/Migalastat Monotherapy and novel ERTs (Enzyme Replacement Therapy). Galafold is an orally administered monotherapy that has full approval in Europe and is ready to be released to the public. Migalastat Monotherapy and Galafold are one in the same, with Galafold being the brand name. While the product is ready for use in Europe, it is still in the approval stages in the Americas and the rest of the world. Amicus’ ERTs for Fabry Disease are in preclinical stages of research.
In addition to Fabry Disease, Amicus Therapeutics studies two other illnesses specifically, Pompe Disease and Epidermolysis Bullosa. Their product for Pompe Disease, a novel ERT named ATB200 and AT2221 are in the middle of the final phase of testing. This treatment will require a chaperone as well. Amicus’ medication for Epidermolysis Bullosa is named SD-101. It is a topical medication. Currently, SD-101 is in the third and final phase of testing.
While Amicus Therapeutics focuses on a few diseases specifically, they also conduct research on other rare diseases and plan treatments for patients with these illnesses. Most of their medications for these various diseases are novel ERTs and most of them are in the primary research phase of development.
Dedicated to research and creating treatments for those with rare illnesses, Amicus Therapeutics is a company to keep an eye on. Several products are nearing their final stages and are one step closer to helping others survive.
More here: Crunchbase

Eva Moskowitz And Her Leadership Of Success Academy

Eva Moskowitz is the CEO of Success Academy, and she has had a distinguished career in education that has brought her to this place. She is leading one of the finest educational companies in America, and she is putting together schools that will serve children well no matter their educational needs. This article explains how Eva has done the work that is required to grow this brand.

 

#1: Eva Moskowitz And Success Academy

 

Eva Moskowitz is known today for being the CEO of Success Academy, and she has spent decades in education working on many levels. She knows how to lead schools that will bring greater success to students, and she uses his public sector and private sector skill set to the table.

 

#2: What Does Success Academy Do?

 

Eva has set up Success Academy to offer personal instruction to the students who count on the school every day. They have opened many schools across America to serve kids who need an alternative education, and Eva often promotes the alternative education that these students needs. She knows that a child who is given a better education today at Success Academy will move on to greater things in the future.

 

#3: How Does Eva Advocate For Her Students?

 

Eva Moskowitz is a name that is known across the education industry for advocating on behalf of all students who need a better education. The students who come to her schools are there because they need to be taught in a new way, and Eva leaves the Success Academy open to as many new educational techniques as possible. She would rather help students learn in a new way than force them to learn in a manner that does not work for them.

 

The career of Eva Moskowitz is one that has made a difference in the lives of thousands of children. The Success Academy is touching lives every day as children learn more than they could have ever imagined in a building that suits them. These children may have the dream of college realized, and Eva will continue to grow this brand to help the alternative student.

Vijay Eswaran of QI Group

Vijay Eswaran is an accomplished entrepreneur, a global motivational speaker, an author, and a philanthropist. He started his early childhood life in Malaysia where his parents lived and worked. Graduating with a socio-economic degree from the London School of Economics, he had odd jobs experience as a construction worker in Belgium, plucked grapes in France, and a cab driver in London.

These odd jobs did not prevent him from obtaining his accounting certification from the Chartered Institute of Management Accountants (CIMA) in the UK and subsequently his Master of Business Administration (MBA) degree from the Southern Illinois University in 1986. Read more: Dato Vijay Eswaran: From taxi driver to worth over $500 million dollars

Vijay Eswaran is the founder and Executive Chairman of QI Group of Companies with various business sectors including wholesale distribution, retailing, hospitality services, education and financial services.

In an interview with ENTREPRENEUR MAGAZINE, Vijay recounted his challenges as an entrepreneur lasting for long several years. “To me, success is as much interwoven with challenges, just as light is to shadow”, he told his interviewer. Vijay describes an entrepreneur as one who is inquisitive, intense, and intuitive. Learn more about Vijay Eswaran: http://philanthropies.org/vijay-eswaran-2/

Vijay Eswaran is revered for his motivational speeches and lectures that touched the lives of individuals around the world. He gave speeches in major universities, business and leadership platforms and spiritual pulpits. He is an author having written 6 books to his credit and regularly writes informative articles for newspapers in Malaysia and Sri Lanka.

A well-known philanthropist, Vijay Eswaran founded RYTHM Foundation (RF), a division of QI Group to promote the group corporate social responsibility plans around the world. He also established Vijayaratnam Foundation in honor of his father in Malaysia.

His foundations work with local NGOs and other charitable organizations on projects in child and youth development, women forum and special education for disabled persons.

According to QBuzz, Vijay Eswaran was adjudged one of Forbes Asia’s Heroes of Philanthropy in 2011. He received the lifetime award in Regional Philanthropy for leading an independent think tank Asia Strategic Leadership Institute in Malaysia. He was also conferred with International Leader in Global Business Strategies award by the Global Organization for People of Indian Origin.